
NCBI . NLM . NIH . GOV {
}
Title[redir]:
RNA-based therapeutics for neurological diseases - PMC
Description:
RNA-based therapeutics have entered the mainstream with seemingly limitless possibilities to treat all categories of neurological disease. Here, common RNA-based drug modalities such as antisense oligonucleotides, small interfering RNAs, RNA ...
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🌠 Phenomenal Traffic: 5M - 10M visitors per month
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Keywords {🔍}
google, scholar, doi, pubmed, pmc, article, free, rna, disease, gene, exon, protein, antisense, aons, delivery, treatment, brain, targeting, aon, splicing, therapeutics, diseases, target, therapy, sirna, expression, muscular, tau, mol, development, ssaons, aptamers, therapeutic, nucleic, dystrophy, clinical, rnabased, neurological, model, mouse, mrna, potential, system, ther, mutations, cell, dmd, patients, drug, oligonucleotides,
Topics {✒️}
spliceosome-mediated rna trans-splicing cell-penetrating peptide conjugates specific cell-penetrating components infusion-related reactions manifesting high-profile tau-targeting treatments α-synuclein antisense oligonucleotides collagen vi-related dystrophy trans-splicing reaction mediated regulate endothelial-mesenchymal transition heparin-binding growth factor tominersen supresses wild-type amido-bridged nucleic acid age-related macular degeneration watson–crick base pairing pro-inflammatory leukocyte infiltration trans-splicing-mediated improvement antisense oligonucleotide-mediated removal antisense 2ʹ-o-methoxyethyl gapmers enhances trans-splicing u7snrna-mediated exon skipping antisense-mediated exon skipping anti-interleukin-17a aptamer display brain-targeting peptides pmc beta search modulate pre-mrna splicing pre-trans-splicing molecule ps-modified antisense oligonucleotides van roon-mom wm wild-type coding sequence small-molecule therapy owing blood-brain barrier penetration intact blood-brain barrier blood-brain barrier damages blood–brain barrier integrity replication-dependent histone mrnas important wild-type function rna-loaded nanoparticle vaccine rna-based drug modalities mediate pre-mrna splicing data availability statement unmodified dna/rna nucleotide thrust rna-based therapeutics rna-based therapeutics set toxic amyloid-β production antisense oligonucleotide-based rescue sirnas targeting β-catenin rna aptamer-based therapeutics rna-induced silencing complex patient-customized oligonucleotide therapy hereditary transthyretin-mediated amyloidosis
Questions {❓}
- Are splicing mutations the most frequent cause of hereditary disease?
- Gene repair by means of trans-splicing: a delicate balancing act between efficiency and specificity?
- How close are miRNAs from clinical practice?
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- Backbone.js
- jQuery
- jQuery module (jquery-3.6.0)
Emails and Hosting {✉️}
Mail Servers:
- nihcesxway.hub.nih.gov
- nihcesxway2.hub.nih.gov
- nihcesxway3.hub.nih.gov
- nihcesxway4.hub.nih.gov
- nihcesxway5.hub.nih.gov
Name Servers:
- dns1-ncbi.ncbi.nlm.nih.gov
- dns2-ncbi.ncbi.nlm.nih.gov
- lhcns1.nlm.nih.gov
- lhcns2.nlm.nih.gov
CDN Services {📦}
- Ncbi